Public Meeting - 30 May 2015

On 30 May 2015 we invited members of the CF community to an event at Imperial College.  We felt it was important that this group was the first to publicly see the results of the multi dose clinical trial.

Now that the data has been published we can share these presentation videos on this page.

Main Results Presentation - Professor Eric Alton (50 min)

02.40: Why was there a delay in releasing the data?
05.10: Gene therapy background
09.00: Clinical programme overview
20.20: The MD trial
25.45: How the trial was analysed
27.50: Adverse events
31.25: Primary outcome results FEV1
34.10: Secondary outcome results
38.50: Results stratified by baseline FEV1
44.10: What do these results mean?
48.50: Thanks

Q&A Session -  Professor Eric Alton & CF Trust Chief Executive Ed Owen (44 min)

  • pGM169

    Find out more about the production of our first clinical product

  • Lab slides

    Find out more about the Tracking Study in 2006

  • Lung Function Test

    Find out more about the preparation for the multi dose trial

  • Staged Nebuliser Delivery

    Find our more about the Single Dose Clinical Trial that started in 2009

  • Staged Gas Transfer

    Find out more about the Multi Dose Trial, following on from the Single Dose Clinical Trial

  • Eric Alton

    Watch the results presentation given by Prof. Eric Alton on 30 May 2015

Find out about the discovery of

the CFTR Gene,

responsible for Cystic Fibrosis

Find out how

the CFTR Gene

causes Cystic Fibrosis

Find out about

the structure of the

CFTR Protein

Why use Gene Therapy

to treat

Cystic Fibrosis?

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